Posts Tagged: clinical trial

Clinical trial into ‘bubble baby disease’ back on track

Baby Evangelina Padilla-Vaccaro on the day she received a gene therapy stem cell transplant.(Photo: UCLAhealth.org)

by DAVID JENSEN posted 02.15.2022

Twenty children seeking treatment for a rare affliction called the “bubble baby disease” today have some big-time, good news concerning a life-saving genetic therapy that they were once denied as the result of a tangled affair that included private profit and the public funding of cutting-edge scientific research.  

UC Davis: First clinical trial of stem cells to treat spina bifida

A stem cell researcher at UC Davis. (Photo: AJ Cheline, UC Davis, via The Stem Cellar)

by DAVID JENSEN posted 03.10.2021

Backed by $17 million in cash from California’s stem cell agency, researchers at UC Davis this month are launching “the world’s first clinical trial using stem cells to treat spina bifida before the child is born.”