Posts Tagged: ADA-SCID

News

California-backed cure for ‘bubble baby’ disease stalls — again

A pipette drops stem cell research fluid on a special container. (Photo: CI Photos, via Shutterstock)

The “bubble babies” saga and a California-financed cure for their life-threatening affliction has hit another snag, more than two years after a British company abandoned the effort. It is a story that involves more than $40 million from California’s stem cell agency, federal regulators, the University of California, the agonizingly slow pace of science and 20 children who have been denied care — not to mention a company called Orchard Therapeutics PLC.

News

Stem cell agency says it’s going all out on ‘bubble baby’ cure

A scientist at work in a biomedical laboratory. (Photo: Tom Robertson, via Shutterstock)

The California stem cell agency says it is doing “everything” it can to move forward on a gene therapy that has saved the lives of more than 50 persons but which has been pushed aside by the company that has exclusive rights to it. The issue has raised questions about the ethics of withholding care from babies and children suffering from a fatal disease.

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